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rare-disease-day-2017-with-a-commitment-to-provide-new-insights-into-rare-diseases Videos
10 videos found
One photographer is helping make special memories for parents of children with rare diseases. “I hope to show the world that babies – and people - with special needs are beautiful and valuable.” ...
Jun. 4, 2022
MPS IVA, also known as Morquio A Syndrome, is a rare disease that affects major organs in the body. Learn more about Morquio A Syndrome from the ...
Mar. 10, 2021
ByBioMarin
At BioMarin, the connection and strong relationships we have with our patients energizes our employees and our company culture every day. Together, we aspire to positively impact the lives of those living with rare diseases. ...
Mar. 10, 2021
ByBioMarin
20 years of rare opportunities. 20 years of personal impact. Despite being faced with potential demise during the company’s infancy, BioMarin persevered to become one of the world leaders in developing therapies for rare genetic diseases. Watch the 20 year journey of the people of BioMarin finding tomorrows by staying focused on the science to make a big difference for small patient ...
Mar. 10, 2021
ByBioMarin
At BioMarin we are tackling scientific problems that no one has worked on before and we are paving the way to develop new scientific discoveries. Learn more from our employees and why they enjoy working at BioMarin. BioMarin is a global biotechnology company focused on developing first-in-class and best-in-class therapeutics that provide meaningful advances to patients who live with serious and ...
Mar. 10, 2021
ByBioMarin
In this video, you will learn more about Philipp’s rare disease and how it has affected his life so far. “Rare", however, is actually not that rare ...
Mar. 10, 2021
The Alliance for Regenerative Medicine’s annual Cell & Gene State of the Industry Briefing, a top-level gathering for key stakeholders in the field. This webinar includes ARM’s annual yearly update on the sector’s progress, followed by two panel sessions featuring top CEOs and executives highlighting future inflection points for cell and gene therapies in the coming year. ...
May. 30, 2022
Paperless | Contact-free | Clinical Research Jeeva is a premium eClinical cloud solution that helps you reach your recruitment and retention targets sooner. Clinical researchers can pre-screen participants, obtain informed consent, enroll subjects, and begin their studies faster by switching from traditional clinical studies to decentralized, remote, and hybrid studies like Jeeva. When you ...
Apr. 26, 2022
Modern drug discovery is inefficient, expensive and risky. On average, there are 2000 failed compounds sitting on pharmaceutical companies shelves, and this number grows at the rate 200 drugs per year. Furthermore, the average costs of a successful drug introduction is a staggering $3bln with an average time-to-market of more than 10 years. This is due to extensive discovery costs including: R&D, ...
Apr. 16, 2021
Explore the latest advancements in modern medicine, from hematocrit determination for precise blood analysis to vein visualization for improved vascular access. Discover cutting-edge intubation equipment and ultrasonic endoscopy revolutionizing surgical procedures. Learn how blood-brain barrier modeling is shaping neurological research and how enzyme replacement therapy offers hope for rare ...
Mar. 12, 2025