More than two decades of people, patients and perseverance

When BioMarin first opened its doors back in 1997, treatment of rare disease was as rare as the conditions themselves. Determined to make a difference, we went on to develop and introduce six first or best-in-class therapies for genetic disorders with limited-to-no treatment options.

Learn more about our history and how we got our start with the short film “Finding Tomorrows.”

You can also read more about our legacy with A Rare Breed.

A Rare Breed recounts the first 20 years of BioMarin’s history, the struggles we faced in developing drugs for little known conditions, and how we grew into a global enterprise. It follows the researchers, patients, and executives who played a role in advancing novel ideas and how they overcame scientific, regulatory, and financial challenges to bring first-in-class and best-in-class therapies to children who needed them.

A Rare Breed is now available on Amazon with all proceeds going to patient advocacy groups focused on rare disease.

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